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John Fielding,
CEO
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Myeloproliferative disorders are rare enough to be considered orphan diseases, which means there is no financial incentive for the big pharmaceutical companies to do research in the field.
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Albert Graham,
Backyard Pool Drainer
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The Rare Disorders category includes diseases and disorders that affect less than 1 percent of the population at any given time.
Noninfectious Diseases Compared to other livestock, llamas are relatively free of digestive disorders Bloat is rare.
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Brian Mengel,
Civil Servant
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It is anticipated that an advisory group to the Office of Rare Diseases will monitor the implementation of these recommendations and provide guidance on future activities.
These rare diseases are a worldwide public health problem and efforts are needed globally to address these problems and to ensure that there is a long-term commitment to support the needed research efforts.
This is especially necessary for rare diseases for which the private sector may not be willing to support or capable of supporting research and product development.
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Arthur Dawkins,
Astro-physicist
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The Office of Rare Diseases and the Center for Scientific Review at NIH should make special efforts to recruit qualified academic scientists in these areas to participate in the grant review process.
Diseases caused by a single gene are relatively rare and so the real impact of genetic screening on public health is likely to come about as more work is done on the genetics of common diseases.
The ORD provides information on rare diseases and conditions and assists in linking research investigators with research subjects and patients who are willing to participate in clinical research investigations.
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David Rosenberg,
Dermatologist
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Rare diseases such as atypical measles and monkey fever as well as such well known disorders as premature aging and allergies have been associated with vaccinations.
Pemphigus is a group of rare autimmune blistering diseases of the skin and/or mucous membranes.
There are already many people with rare diseases and disorders that go untreated because the treatment is not "profitable.
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